PIPELINE
RESEARCH
CATEGORY
Parkinson’s disease
Parkinson’s disease is a progressive neurodegenerative disease that usually develops at 40–70 years of age, with major signs of dyskinesia […]
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Amyotrophic Lateral Sclerosis（ALS）
Amyotrophic lateral sclerosis (ALS) is a neurodegenerative disease that selectively affects motor neurons and has no known cause or treatment. […]
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Alzheimer’s disease
We incorporate the gene that encodes an enzyme that decomposes amyloid-β peptides (Aβ) into a virus vector that only expresses […]
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Molecular Imaging
To complement the gene therapy, we are applying molecular imaging technology to diagnose symptoms and to evaluate the effects of […]
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AAV vector platform
Broad intellectual property around two original AAV vectors (AAV.GTX and AAV.GT5) with in vivo proof of concept data Potential out-licensing […]
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In-house Manufacturing Facility
Two years of gene therapy manufacturing expertise First GCTP/cGMP/PICS GMP complied manufacturing facility with 200L bioreactor completed Mar 2017 The […]
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